This website uses cookies to ensure you have the best experience. Learn more

Gene Therapy And Genetic Disorders Essay

1397 words - 6 pages

Every cell in the human body is given instruction by our genes as to what job each cell should perform. Every tiny detail is dependent upon the instruction of our genes. If a gene or cell becomes damaged, changes, or is missing, there are major consequences to the body and the health of the individual. Genetic disorders are caused by damaged or missing genes and can be life threatening. They can lead to serious diseases in the individual. Certain types of genetic disorders cannot be cured by treatment with medicine. Drugs may help relieve symptoms of certain disorders but cannot cure the disease. Drugs cannot reverse or repair a damaged cell or gene. Scientists and doctors have done extensive research to find ways to reverse the negative effects of a damaged gene or repair a missing or damaged gene in order to cure diseases. This led to the discovery of gene therapy. Gene therapy’s main focus is on replacing or repairing defective genes within the body in the hope that this will repair the defect in the gene and in doing so cure or at least lessen the negative effects of the disease. The procedure involves the introduction of a healing or working gene copy into specific cells of an individual in order to repair or replace a damaged gene. Two main methods have been tried —adding a gene to substitute for a gene that wasn't working as it is supposed to be, or changing genes that are not working properly. Cystic fibrosis, hemophilia and sickle cell anemia are among the diseases where gene therapy has been considered. Diseases that are incurable in which gene therapy has also been considered include Parkinson’s, HIV/AIDS, Alzheimer’s, diabetes, cancer, and heart disease.
There are two types of gene therapy. The first, somatic gene therapy involves the transfer of healthy genes into the physical cells of an infected patient. These cells include every cell type in the human body except for the cells which make up the sperm and ova and certain types of stem cells. Somatic cells cured by gene therapy may reverse the symptoms of the diseased individual but the changed gene is not inherited by the offspring of that individual. The second type of gene therapy, genetic gene or germ line therapy, involves the manipulation of the germ cells or the sperm or eggs of the patient. The changed genes of the germ/sperm/ova cells then are able to be inherited by future generations of the patient. Genetic gene therapy can be used to treat genetic disorders.
The passing down of ones traits to their offspring – whether it be eye color or a genetic disease is the reason that genetic gene therapy is the subject of ethical controversy, as opposed to somatic gene therapy. There is little ethical controversy regarding somatic gene therapy since it is treating a specific infected patient and the effects of the therapy begin and end...

Find Another Essay On Gene Therapy and Genetic Disorders

Cystic Fibrosis And Gene Therapy Essay

1337 words - 5 pages recombinant DNA methods were successfully used. Since then development of techniques that allow geneticists to locate the position of genes has led to a greater understanding of the causes of genetic disorders. Now scientists are able to consider treating people with genetic disorders by introducing normal genes into body cells. Gene therapy has been successfully used in a few cases and many more genetic disorders are currently being investigated. The

Genetic Disorders and Down Syndrome Essay

1177 words - 5 pages A genetic disorder is a disease that is caused by an abnormality in an individual's DNA. Abnormalities can range from a small mutation in a single gene to the addition or subtraction of an entire chromosome or set of chromosomes” (Letsou). Most individuals are either related to or know someone who is effected by some type of disability. Many of these disabilities are caused by genetic disorders. Genetic disorders may alter physical appearance

The Pros and Cons of Gene Therapy

2200 words - 9 pages infected with the virus vector. The vector then unloads its genetic material (which contains the needed correct genes) to the target cell. The correct gene is then able to generate the correct functional protein and so restores the target cell to the normal state. ( The reason why carrier molecules are usually needed is because otherwise correct genes could only be inserted in certain tissues

Implications of and Attitudes toward Gene Therapy

2223 words - 9 pages the best systems to deliver genetic materials to cells still remain. These are the main obstacles in making gene therapy a legal and effective treatment. It is a controversial issue that has polarised opinions on it. I believe that gene therapy is the future of incurable diseases. Although the techniques are far too risky, it could still be considered as a successful prospect in the future. There could still be improvement on the present

Gene Therapy and Its Effect on Cancer

3602 words - 14 pages therapy deliberately introduces genes into the human cells to compensate for aberrant genes that cause genetic disease" (Beese, 1996). This therapy can be administered in two ways. One is germ-line therapy which not only treats the cells of that individual but these treated cells could be passed onto the individual's offspring. This type is the focus of much of the opposition of gene therapy itself because trials take many years and few results have

Advantages and Disadvantages of Gene Therapy

1623 words - 6 pages cells had been implemented with a new functional gene, they were injected back into the patient thus relieving the symptoms and providing Ashanti with proper white blood cell counts and plenty of ADA. The solution unfortunately isn’t a permanent one so the experiment had to be repeated several times a year, but at least this shows some promise is obtaining a resolution. Another approach of gene therapy has been tried on a genetic disease of

Gene Therapy and its Potential to Cure Deafness

1418 words - 6 pages , making it valuable in the slow steps of finding an eventual cure. References Coghlan, A (2005, February) Gene Therapy is first deafness ‘cure.’ New Scientist. 7/25/05: Houbebine, Louis-Marie. (2003). Animal transgenesis and Cloning. Chichester: The Atrium Maugh, T. (2005, February) Gene therapy fixes animal hearing. Los Angeles Times. Pau, H., r.w. Clarke. (2004). Advances in the genetic manipulations

Gene Therapy for Multiple Sclerosis, Cancer, and Sickle Cell Diseases

731 words - 3 pages , it is class of diseases characterized by out-of control cell growth. Currently there is around 100 different types of cancer. In current times some forms of cancer are already curable but some are only curable up to certain stages. Currently in the word there is around 13.5 million diagnosed with cancer. It will benefit the whole world if gene therapy is able to cure cancer. Many people lives will be saved and we will be done with this dreaded

Genetic Disorders and they become what they are

1424 words - 6 pages parents. When genes are passed to offspring diseases are also sometimes past to cause genetic disorders. Genetic Disorders are a mutation in a gene. Mutations are changes in the DNA sequence and can happen anytime, from being a single cell to being 100 years old. There are several type of genetic mutations that occur, chromosome abnormalities, single- gene disorder, multifactorial disorder, and mitochondrial disorder.Chromosome abnormalities occurs

Report on Behavioral Therapy Psychology and its effects on Depressions and disorders. Behavioral therapy

926 words - 4 pages Behavior TherapiesThere are many therapies that are used in the treatment of psychological disorders although one stands above the rest, behavioral therapy. Behavioral therapies "focus only on changing a person's specific behavior in the present day" (Nolen-Hoeksema, 2004, pg. 146). "Research clearly indicates that the behavior of humans is best understood and ultimately managed by comprehensive strategies and techniques that consider not only

Critique of 'The ethics of Human Gene Therapy' by L Walters and J Gage Palmer

947 words - 4 pages IntroductionThe article 'The Ethics of Human Gene Therapy' by L Walters and J Gage Palmer is a report of the first human gene therapy experiments, and the ethical issues surrounding it. It is an account of the lives of the people -particularly two young girls- who received the therapy and the associated outcomes and impacts it had, both on her and her family's life, and that of the general public.A major part of the article presents seven

Similar Essays

Gene Therapy: How Will It Change The Future Of Genetic Disorders

2179 words - 9 pages completion of the human genome was on all the major news wires, televisions and newspapers. What does it mean though? How will this help mankind? One area to which this knowledge can be applied is in the area of gene-therapy. Gene-therapy is now being tested to treat and cure some common genetic disorders. Like all new research, gene-therapy is the center of much controversy. A discussion of genetic disorders and current prevention methods is

Genetic Engineering: The History Of Gene Therapy

892 words - 4 pages genetic disorders could be cured. Four thousand genetic conditions have been found to be linked to a single gene. By replacing that mutant gene, genetic disorders would cease to exist. As of early 1998, around 250 gene therapy trials were being conducted around the world. Overall, one would think it’d be safe to say that that task doesn’t seem too hard at all, the only thing you need to do is replace the gene. That seems simple enough. In

Genetic Engineering: Power Of Gene Therapy

807 words - 3 pages The Power of Gene Therapy Each day as our technology advances, we become aware of new diseases and disorders. We also find effective ways to alleviate a number of these problems. In the last decade, gene therapy has been found to treat a portion of life-threatening illnesses such as Cystic Fibrosis, Severe Combined Immune Deficiency (SCID), and Alzheimer's disease. Cystic Fibrosis (CF) is a genetic disease that affects the exogenous

Gene Therapy And Genetic Engineering: Should It Be Approved In The Us?

3126 words - 13 pages receiving the treatment the patients' scores on movement tests improved on average by 30 percent.(Gene Therapy Special News Items, 1.)” Genetic engineering, and its form dealing with humans, gene therapy, is a process in which genes are replaced or "tweaked" to acquire a certain trait or cure an illness or disease. This can be performed in the fetal stage through adulthood. While genetic engineering and gene therapy can help prevent disease and